Cas13d for Ube3a-ATS Targeting in Angelman Syndrome

Beitnere, U; Palomares, MS; O'Geen, H; Deng, PB; Cameron, DL; Adhikari, A; Fenton, TA; Copping, NA; Silverman, JL; Fink, KD; Segal, DJ

MOLECULAR THERAPY, 2021; 29 (4): 269